URMC one of first in US to offer new gene replacement therapy

URMC one of first in US to offer new gene replacement therapy

URMC has been tapped as one of the first institutions in the U.S. to offer a new gene replacement therapy to treat spinal muscular atrophy (SMA). Until a few years ago, an SMA diagnosis was tantamount to a death sentence. Learn how this cutting-edge therapy is transforming the lives of patients and their families.

To read the latest about all of what Rochester helps make possible, please visit the University’s Newscenter here and the Medical Center’s Newsroom here.



More Stories